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At $2.1 million, newly approved Novartis gene therapy will be world’s most expensive drug

At $2.1 million, newly approved Novartis gene therapy will be world’s most expensive drug

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  • “The issue with many of these drugs is that they are expensive but also life-changing for those who need them...”

    The “issue” behind the astronomical price is actually issues: Cost of development which includes prior acquisition of the company who first developed the drug); drug production - biologicals

    “The issue with many of these drugs is that they are expensive but also life-changing for those who need them...”

    The “issue” behind the astronomical price is actually issues: Cost of development which includes prior acquisition of the company who first developed the drug); drug production - biologicals are not cheap to reproduce in quantity; limited patient pool - this is a rare disease; length of treatment - one and done, no years of patients taking medication to recoup the money invested in development. The high cost is not because a medication is life saving - so is CPR and that’s free. It is a cold, actuarial decision when they name the price. For all the heart medication they produce, I wonder if Novartis has one.

  • Comes back to the same issue that was discussed a couple of weeks ago in another article:

    https://share.qz.com/news/2425049

    And it's still early days, so really we don't know if a single application is going to be sufficient, nor do we know any of the potential side effects or unintended consequences

    Comes back to the same issue that was discussed a couple of weeks ago in another article:

    https://share.qz.com/news/2425049

    And it's still early days, so really we don't know if a single application is going to be sufficient, nor do we know any of the potential side effects or unintended consequences. The breakthroughs that are possible are important to pursue for innovation in medical science. But there are risks in the same way as the CRISPR work could be misused to produce children immune to HIV, Ebola, bubonic plague or even a super race or genetically enhanced war machine soldier. It is absolutely critical that there is a governance framework and a body of ethics for the industry to follow with policing.

  • This is priceless: « In some cases, the treatment is being given to children at six weeks of age, highlighting how soon after birth a child’s genes can be fixed. »

  • The high cost of drugs in the United States is not really due to development costs, as much of those costs are covered by government funding and research grants. Marketing is a huge and arguably unethical expenditure that is legally allowed in only a handful of developed countries, including the US.

  • I understand everyone (Big Pharm) and little pharm, all the ones who care very much and work so hard to just have these meds available to those who need it, and all others in between work and spend millions, spend loans, grants, University backing and Lord knows how else! They all need to get that money

    I understand everyone (Big Pharm) and little pharm, all the ones who care very much and work so hard to just have these meds available to those who need it, and all others in between work and spend millions, spend loans, grants, University backing and Lord knows how else! They all need to get that money back, and for sure they will and MORE! In America 1 in 50 are carriers. Just in America. That’s counting 6 million people. 1 in 10,000 children will be born with a type of AMS. Right now as recorded with the smafoundation.org there are 9,000 cases in the United States only. If they decided to make this affordable to all families going through this devastating ordeal with their children of course they would make their mark and profit! I just see a child suffering in a hospital with a feeding tube and a respirator because his muscles cannot help his lungs breathe anymore and the child’s family are surrounding her, helpless, without any hope. The only hope they had was a new injection! It was helping all other kids!! The price of an injection though was unreachable for this family. Their church helped them as well as so many of their friends and family but they never even came close to buying one injection! Meanwhile, in another room, another family with a child who also was diagnosed with AMS, is going home! He is off his feeding tube and can breathe on his own! He is getting stronger everyday! It’s wonderful! His family was able to afford Novartis and he just received the injection 2 weeks ago....

  • So expensive as to be unaffordable. "Novartis is likely to face backlash from critics who believe charging millions of dollars for any medicine — no matter how effective — renders it unaffordable for a healthcare system already under financial stress."

  • #Breaking: there’s a new approval from the FDA about Novartis getting approval for genetics therapy. This would mean a lot for mx given the closure of both countries and its genetic characteristics

  • Okay...I get that the pharmaceutical maker put tons of money into research and development for this drug and they have to recover those costs. I'm not sure of how much of that money came from public grants or the taxpayer. However, I feel there has to be a better way than when you end up with a life-saving

    Okay...I get that the pharmaceutical maker put tons of money into research and development for this drug and they have to recover those costs. I'm not sure of how much of that money came from public grants or the taxpayer. However, I feel there has to be a better way than when you end up with a life-saving drug that costs millions. This is absolutely disgusting.

  • Who can afford such an expensive medication?

  • This is why unconditional universal healthcare is needed in the USA.

  • On Friday, May 24, Novartis won approval for the drug and set the price at $2.125 million, making it the world's most expensive one-time drug ever.